Rare Disease Jobs

Scholar Rock is hiring a Senior Director of Patient Marketing to own U.S. patient and caregiver strategy and execution for apitegromab’s launch and commercialization in spinal muscular atrophy.

Lead regional Thought Leader engagement and advocacy partnerships to shape commercial strategy and support launch activities for ANI’s rare disease product.

An accomplished commercial leader is needed to recruit, develop, and lead regional sales teams to successfully launch and grow specialty biotech therapies across the U.S.

Senior market access leader needed to develop and execute payer strategies and launch readiness for rare neurology therapies, with responsibility for cross-functional alignment and patient access outcomes.

Experienced market-access leader needed to drive national payer strategies and contracting for Ascendis Pharma’s portfolio to ensure formulary placement and patient access under pharmacy benefit channels.

Acadia seeks an experienced, territory-based Senior Area Business Manager to drive specialty sales and stakeholder engagement across New England for its FDA‑approved Rett syndrome treatment.

Represent a patient-centered biopharma company as a field-based Pharmaceutical Sales Representative promoting specialized rare-disease products to Primary Care physicians across an assigned U.S. territory.

Represent a patient-focused pharmaceutical company as a field-based Sales Representative promoting cardiology and rare-disease therapies to primary care physicians.

Lead the development and execution of Cure HHT’s patient education initiatives and conferences to inform, connect, and empower the HHT community.

Lead U.S. KOL engagement and peer-to-peer education for Ascendis Pharma’s endocrine portfolio, managing a team of Thought Leader Liaisons and delivering strategic, compliant congress and speaker programs.

Senior regulatory leader needed to lead Sobi’s Global Advertising & Promotion team, drive regulatory strategy and FDA interactions, and own the global review process for promotional and corporate materials.

Ascendis Pharma is hiring a strategic Senior Director to lead U.S. Key Opinion Leader engagement and congress/speaker bureau strategy for its endocrine portfolio while managing a team of Thought Leader Liaisons.

Senior commercial executive needed to lead global sales, marketing, and business development for a cutting-edge radiopharmaceutical portfolio with responsibility for strategy, pricing, and partner relationships.

Experienced clinical project manager needed to lead global trials and coordinate Data Monitoring Committee activities for a CRO servicing pharma, biotech, and device sponsors.